Trending Articles

article thumbnail

STAT+: Cogent Biosciences drug improves symptoms of chronic immune disorder, study results show

STAT

Cogent Biosciences said Monday that its experimental drug reduced the symptoms of a chronic immune disorder called indolent systemic mastocytosis. The results mean the drug achieved the goals of a Phase 3 study, but a comparison to a rival treatment from Blueprint Medicines remains muddled.  In its study, Cogent’s drug, called bezuclastinib, showed a 24-point improvement in a patient-reported symptoms score, compared to a 15-point improvement for participants given a placebo.

article thumbnail

Pricing watchdog will take on the rising cost of drugs at launch

PharmaVoice

ICER’s upcoming report could shed light on how the launch price of newly approved drugs affects overall cost and access from a patient perspective.

147
147
Insiders

Sign Up for our Newsletter

This site is protected by reCAPTCHA and the Google Privacy Policy and Terms of Service apply.

article thumbnail

As its cancer vaccine moves through the clinic, Transgene sets sights on manufacturing

PharmaVoice

Skip to main content CONTINUE TO SITE ➞ Dont miss the most important voices in pharma Let PharmaVoices free newsletter keep you informed on what industry leaders are saying, straight from your inbox. By signing up to receive our newsletter, you agree to our Terms of Use and Privacy Policy. You can unsubscribe at anytime. Voices Q&A Profiles Biotech Spotlight First 90 Days Opinions Topics Biotech Commercialization Leadership Manufacturing Patient Pharma Policy & Regulation Research & Deve

Vaccines 179
article thumbnail

BiomX phage therapy shows potent effect in cystic fibrosis trial

Pharma Times

Subscribe Advertise About us Follow Follow Follow Follow GO Magazine PharmaTimes Magazine Archive Web Exclusives News Competitions Appointments Business Insights Webinars Thought Leadership BiomX phage therapy shows potent effect in cystic fibrosis trial by John Pinching | 9th Jul 2025 | News BX004 achieves 500-fold bacterial reduction with no resistance in phase 1b/2a study BiomX has published promising phase 1b/2a trial results in Nature Communications , demonstrating that its phage cocktail B

article thumbnail

Navigating Payroll Compliance: Future-Proofing Payroll in an Evolving Regulatory Landscape

Speaker: Jennifer Hill

Payroll compliance is a cornerstone of business success, yet for small and midsize businesses, it’s becoming increasingly challenging to navigate the ever-evolving landscape of federal, state, and local regulations. Mistakes can lead to costly penalties and operational disruptions, making it essential to adopt advanced solutions that ensure accuracy and efficiency.

article thumbnail

Veeda Lifesciences invests in Mango Sciences to integrate AI into global clinical trial operations

Express Pharma

Veeda Lifesciences, a global contract research organisation (CRO), has announced an investment in Mango Sciences, a Boston-based healthcare AI and data company. The investment is part of Veeda’s strategy to integrate artificial intelligence into its clinical trial operations, with a focus on improving patient recruitment, trial efficiency, and diversity across global markets.

More Trending

article thumbnail

Child walks again after receiving experimental treatment for rare genetic condition

STAT

In what experts are calling a “dream come true,” scientists used a recent biochemical discovery to help an 8-year-old boy with a rare genetic condition regain mobility. Researchers from NYU Langone demonstrated, in a study published in Nature on Wednesday , how a chemical precursor to a commonly available enzyme, CoQ10, can help brain cells overcome a rare genetic condition that severely hobbles cells’ energy production process.

324
324
article thumbnail

Drugmakers Notch a $5 Billion Win in Republicans’ Policy Bill

NY Times

More medicines will be spared from Medicare price negotiations, a change that is projected to wipe out billions in savings for the federal government.

94
article thumbnail

Fette Compacting India and Goa College of Pharmacy join hands to upskill Goa pharma students

Express Pharma

Fette Compacting India, a global leader in tablet production technology, has signed a Memorandum of Understanding (MoU) with Goa College of Pharmacy to upskill students and prepare them for careers in the pharmaceutical industry. The agreement was signed at Goa College of Pharmacy’s campus in Panaji by Ashok Gourish, Managing Director of Fette Compacting India, and Dr Gopalkrishna Rao, Principal of Goa College of Pharmacy.

83
article thumbnail

Pharmacies’ clinical services offering to expand under NHS 10-year plan

The Pharmacist

The government has pledged to ‘transition’ community pharmacy from a dispensing-focused service to offering more clinical services, as part of its long-awaited NHS 10-year plan. Published today, the 168-page blueprint has committed to increasing the role of community pharmacy in the management of long-term conditions, including treatment of obesity, high blood pressure and high cholesterol. […] The post Pharmacies’ clinical services offering to expand under NHS 10-year plan appeared first

article thumbnail

From Diagnosis to Delivery: How AI is Revolutionizing the Patient Experience

Speaker: Simran Kaur, Founder & CEO at Tattva Health Inc.

The healthcare landscape is being revolutionized by AI and cutting-edge digital technologies, reshaping how patients receive care and interact with providers. In this webinar led by Simran Kaur, we will explore how AI-driven solutions are enhancing patient communication, improving care quality, and empowering preventive and predictive medicine. You'll also learn how AI is streamlining healthcare processes, helping providers offer more efficient, personalized care and enabling faster, data-driven

article thumbnail

Leading medical groups sue Kennedy over changed Covid-19 vaccine recommendations

STAT

WASHINGTON — Six major medical groups, and a pregnant physician, are suing health secretary Robert F. Kennedy Jr. over changes he made to Covid-19 vaccine recommendations that they say were unlawful and undermine public trust in health care. The suit argues that a May 19 directive signed by Kennedy, which said that the Covid-19 vaccine would no longer be recommended for healthy children and pregnant people , violates decades of policy governing how vaccines are reviewed, approved, an

Vaccines 363
article thumbnail

The MEK effect on cancer — a slow and steady approach to drug resistance

PharmaVoice

Skip to main content CONTINUE TO SITE ➞ Dont miss the most important voices in pharma Let PharmaVoices free newsletter keep you informed on what industry leaders are saying, straight from your inbox. By signing up to receive our newsletter, you agree to our Terms of Use and Privacy Policy. You can unsubscribe at anytime. Voices Q&A Profiles Biotech Spotlight First 90 Days Opinions Topics Biotech Commercialization Leadership Manufacturing Patient Pharma Policy & Regulation Research & Deve

Immunity 130
article thumbnail

Patients with ultra-rare diseases worry new FDA rules will leave them without treatment

The Guardian - Pharmaceutical Industry

Testing is difficult for drugs for rare diseases, and new rules may make it harder for sufferers to obtain life-saving drugs US drug regulators have increasingly signaled a focus on faster approvals and rare diseases, but patients with ultra-rare ailments fear they are falling through the cracks, especially given challenges to conducting clinical trials.

85
article thumbnail

Clearsynth receives government backing to advance India’s deuterated chemical production

Express Pharma

Clearsynth Labs has obtained grants from the Technology Development Board (TDB), which is part of the Department of Science and Technology (DST), Government of India, to build a dedicated manufacturing facility for the commercial-scale production of deuterated reagents, intermediates, and building blocks. This is a significant step towards enhancing India’s capabilities in advanced specialty chemicals.

article thumbnail

Why Every Small Business Needs an HCM Solution: A Comprehensive Guide

Managing HR tasks like payroll, compliance, and employee data can overwhelm small businesses. That’s where a Human Capital Management (HCM) solution comes in. Our eBook, Why Every Small Business Needs an HCM Solution: A Comprehensive Guide , shows how an HCM system automates tedious processes, ensuring your business stays compliant and efficient. You’ll learn how to simplify payroll, eliminate costly errors, and empower your employees with self-service tools.

article thumbnail

Boehringer raises hope of oral drug for diabetic eye disease

pharmaphorum

Boehringer has started a phase 2 trial of an oral therapy that could help people with diabetic macular oedema avoid regular injections into the eye

article thumbnail

STAT+: A GPT-powered medical device certified in Europe raises questions about generative AI in health care

STAT

Last fall, a group of experts advising the U.S. Food and Drug Administration debated for two days on how to regulate generative artificial intelligence tools in medicine. One report presented at the meeting showed that a generative AI tool supposedly used by 40% of the radiology practices in the U.S. produced clinically significant errors in one of every 21 reports.

327
327
article thumbnail

GLP-1 roadblocks: Discontinuation rates soar as insurers clamp down

PharmaVoice

Skip to main content CONTINUE TO SITE ➞ Dont miss the most important voices in pharma Let PharmaVoices free newsletter keep you informed on what industry leaders are saying, straight from your inbox. By signing up to receive our newsletter, you agree to our Terms of Use and Privacy Policy. You can unsubscribe at anytime. Voices Q&A Profiles Biotech Spotlight First 90 Days Opinions Topics Biotech Commercialization Leadership Manufacturing Patient Pharma Policy & Regulation Research & Deve

article thumbnail

‘Every year we pay more’: Main Line CEO on the push to cut costs

Beckers Hospital Review

Weeks into his new role as president and CEO of Bryn Mawr, Pa.-based Main Line Health, Edward Jimenez told Becker’s the five-hospital system — with more than 13,000 employees — is taking steps to stay financially resilient while also hiring more physicians and planning new care sites to improve access. Mr. Jimenez assumed the top leadership role in June and brings nearly 30 years of healthcare leadership experience.

article thumbnail

Best Practices to Streamline Compensation Management: A Foundation for Growth

Speaker: Joe Sharpe and James Carlson

Payroll optimization can be one of the most time-consuming and complex factors of small business management. Yet, organizations that crack the code on streamlining employee compensation often discover innovative avenues for growth. With the right strategies in place, outsourcing and streamlining payroll processes can result in substantial time and resource savings.

article thumbnail

Pulmonary arterial hypertension market to reach $9.3 bn in 7MM by 2034

Express Pharma

The pulmonary arterial hypertension (PAH) market across the seven major markets (7MM*) is poised to grow at a compound annual growth rate (CAGR) of 2.0 per cent from $7.6 billion in 2024 to $9.3 billion in 2034, driven by the adoption of triple combination therapy, novel prostacyclin formulations, and the entry of disease-modifying therapies, according to GlobalData.

article thumbnail

Pharma welcomes EU push to restore life sciences sector

pharmaphorum

European pharma trade group EFPIA has said that a strategy launched by the EU to bolster the region's standing in life sciences is a "step forward.

71
article thumbnail

U.S. sees most single-year measles cases since it declared disease eliminated

STAT

The United States has now recorded more confirmed measles cases this year than in any year in well over a quarter-century — and 2025 is only just past the halfway mark. On Wednesday, the Centers for Disease Control and Prevention reported that the number of confirmed measles cases in the country had risen to 1,288, exceeding the 1,274 cases reported in 2019, to become the highest single-year total since the United States declared measles eliminated in 2000.

363
363
article thumbnail

Is biopharma dealmaking getting hot again?

PharmaVoice

Skip to main content CONTINUE TO SITE ➞ Dont miss the most important voices in pharma Let PharmaVoices free newsletter keep you informed on what industry leaders are saying, straight from your inbox. By signing up to receive our newsletter, you agree to our Terms of Use and Privacy Policy. You can unsubscribe at anytime. Voices Q&A Profiles Biotech Spotlight First 90 Days Opinions Topics Biotech Commercialization Leadership Manufacturing Patient Pharma Policy & Regulation Research & Deve

Packaging 130
article thumbnail

Enhance Healthcare Efficiency With Top Payroll & HCM Services

Running a healthcare facility requires precision and care, not just for patients but also for your staff. Our guide, "A Buyer’s Guide to Payroll & HCM Services," helps healthcare providers choose the best provider. Efficient payroll management ensures timely, accurate payments, critical for maintaining staff morale and trust. Compliance support helps navigate complex healthcare regulations and avoid costly fines.

article thumbnail

ASBM Announces Retirement of Doug Badger,Welcomes Beato and Downing to Board

Safe Biologics

ARLINGTON, VA — July 7, 2025 — The Alliance for Safe Biologic Medicines (ASBM) today announced the retirement of longtime Board member Doug Badger, and the appointment of two new members to its Board of Directors: Cristina V. Beato, MD, and Chris Downing, both of whom previously served in senior leadership roles at the U.S. Department of Health and Services (HHS) from 2001 to 2008.

113
113
article thumbnail

CDC’s vaccine advisory committee overhaul raises concerns for vaccine oversight: GlobalData

Express Pharma

On June 9, 2025, in a significant and controversial shake-up, US Secretary of Health and Human Services Robert F. Kennedy Jr. dismissed all 17 members of the Centers for Disease Control and Prevention (CDC) Advisory Committee for Immunization Practices (ACIP), the body responsible for advising the federal government on vaccine safety. This decision has raised alarms among public health experts and stakeholders in the vaccine development community, says GlobalData.

article thumbnail

VarmX secures US approval to begin phase 3 trial of urgent surgery treatment

Pharma Times

Subscribe Advertise About us Follow Follow Follow Follow GO Magazine PharmaTimes Magazine Archive Web Exclusives News Competitions Appointments Business Insights Webinars Thought Leadership VarmX secures US approval to begin phase 3 trial of urgent surgery treatment by John Pinching | 8th Jul 2025 | News New trial to test VMX-C001’s effectiveness in restoring coagulation in FXa DOAC patients Biotech company VarmX has received clearance from the US FDA to begin a phase 3 trial of its lead candida

82
article thumbnail

Mattel introduces its first Barbie with type 1 diabetes

STAT

NEW YORK — Mattel has introduced its first Barbie representing a person with type 1 diabetes, as part of wider efforts from the toy maker to increase inclusivity among its dolls. In an announcement Tuesday, Mattel  said  it had partnered with Breakthrough T1D — a type 1 diabetes research and advocacy organization formerly known as Juvenile Diabetes Research Foundation, or JDRF — to ensure that the design of the doll “truly captures the community.

Diabetes 288
article thumbnail

Position Your Pharmacy for Expansion

Speaker: Chris Antypas and Josh Halladay

Access to limited distribution drugs and payer contracts are key to pharmacy expansion. But how do you prepare your operations to take the next step? Meaningful data: Collect and share clinical data regarding outcomes, utilization, and more Reporting: Limited distribution models require efficient tracking and reporting systems Workflows: Align workflows with specific pharma and payer contractual requirements For in-depth, expert insights on pharmacy expansion, watch this webinar from Inovalon.

article thumbnail

Generative AI Can Design Drugs. But Can It Own Them?

Drug Patent Watch

"The Future of Pharma is in Flux: Can AI-Designed Medicines Be Owned? As the pharmaceutical industry grapples with the rise of generative AI, a new question is emerging: who owns the rights to medicines designed by machines? In a groundbreaking development, researchers have successfully used AI to design novel compounds with unprecedented efficacy.

article thumbnail

A rapid microbiological method case study for advanced therapy medicinal products

European Pharmaceutical Review

Embedded as the cornerstone of microbiological quality are processes that have remained the same for over a century, unchanged from their early beginnings. To achieve optimal detectability and considerably lower risk to patients, the traditional sterility test requires a minimum of 14 days of incubation, and sometimes even longer if the test sample renders media turbid and subculturing is required to overcome visual interference.

article thumbnail

Lupin launches Ipratropium Bromide Nasal Solution (Nasal Spray), 0.03 per cent and 0.06 per cent in the US

Express Pharma

Lupin announced the launch of Ipratropium Bromide Nasal Solution (Nasal Spray), 0.03 per cent and 0.06 per cent, in the United States. Ipratropium Bromide Nasal Solution (Nasal Spray), 0.03 per cent and 0.06 per cent are bioequivalent to Atrovent Nasal Spray, 0.03 per cent and 0.06 per cent, of Boehringer Ingelheim Pharmaceuticals. Ipratropium Bromide Nasal Solution (Nasal Spray) 0.03 per cent is indicated for the symptomatic relief of rhinorrhea associated with allergic and nonallergic perennia

78