Nitisinone Becomes First and Only FDA-Approved Treatment for HGA in Adults With AKU
Pharmacy Times
JUNE 19, 2025
With this action, nitisinone is the first and only FDA-approved treatment for AKU. 1 AKU, also known as black urine disease, is a rare inherited disorder that prevents the patient’s body from completely breaking down 2 amino acids, tyrosine and phenylalanine.
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