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Realising milestones with gene therapy for SMA

European Pharmaceutical Review

3 The one-time gene therapy received final draft guidance from the National Institute for Health and Care Excellence (NICE) on 16 March 2023. 1 This is assuming a $1M price tag for all gene therapies. Health Resources – pharmaceutical spending – OECD Data [Internet] [cited 2023Apr]. cited 2023May].

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Oslo Medicines Initiative asks how to balance innovation incentivisation with security of access

pharmaphorum

“Access to medicines remains one of the most challenging policy areas in every country we work with through the pan-European region,” said Natasha Muscat, Director of Country Health Policies and Systems at World Health Organization (WHO) Europe. WHO is OMI? And that’s exactly what the OMI is setting out to do. About the author.

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Risk-sharing agreements are growing at a rate of 24%

Pharmaceutical Technology

This is not the first treatment to come with a high price tag. On November 22, 2022, the FDA approved CSL Behring’s Hemgenix (etranacogene dezaparvovec), the first gene therapy treatment for hemophilia B, with a staggering manufacturer price of $3.5

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FDA slammed over Aduhelm OK as Biogen takes heat for $56k price tag

pharmaphorum

That was the damning conclusion of the influential Institute for Clinical and Economic Review (ICER) in the US to yesterday’s approval of Aduhelm (aducanumab), the first new treatment for Alzheimer’s since 2003, which it says has “no evidentiary basis.” billion in 2027.

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How data is crucial to the relaunch of the Cancer Moonshot

pharmaphorum

During the first stage of the initiative, more than 2,000 research papers were published, 49 clinical trials were carried out, and more than 30 patents were filed through the support of the US National Cancer Institute (NCI). Building a bank.

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The “Medical Bypass”: new drugs to strike obesity

Pharmaceutical Technology

The Health Survey for England 2019 reported that 28% of adults in the UK were obese and 36.2% A 2017–2018 National Health and Nutrition Examination Survey (NHANES), showed that 30.7% A 2017–2018 National Health and Nutrition Examination Survey (NHANES), showed that 30.7% were overweight but not obese.

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The “Medical Bypass”: new drugs to strike obesity

Pharmaceutical Technology

The Health Survey for England 2019 reported that 28% of adults in the UK were obese and 36.2% A 2017–2018 National Health and Nutrition Examination Survey (NHANES), showed that 30.7% A 2017–2018 National Health and Nutrition Examination Survey (NHANES), showed that 30.7% were overweight but not obese.